Fast Five Quiz: Treatment of Hereditary (Familial) Transthyretin-Related Amyloidosis (hATTR)

Jefferson R. Roberts, MD; Victoria M.F. Mank, MD


February 05, 2021

Hereditary (familial) transthyretin-related amyloidosis (hATTR) is a rare, severely debilitating, and often fatal disorder caused by a mutation in the gene encoding transthyretin (TTR). It results in abnormal amyloid protein buildup in multiple organ systems, leading to progressive peripheral neuropathy, cardiomyopathy, nephropathy, and gastrointestinal dysfunction. Due to the multiorgan system involvement of the disease, an interdisciplinary approach to treatment is crucial to manage all comorbidities. Available treatment modalities include surgical and pharmacotherapeutic options.

How much do you know about the treatment of hATTR? Test your knowledge with this quick quiz.


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